BridgeBio aces phase 3 rare disease test, clearing path to FDA | Hacker News

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		BridgeBio aces phase 3 rare disease test, clearing path to FDA (fiercebiotech.com)
		1 point by randycupertino 43 days ago \| hide \| past \| favorite \| 1 comment

randycupertino 43 days ago [–]

Exciting results for this rare genetic muscle-wasting disorder Limb-Girdle Muscular Dystrophy (LGMD2I/R9) trial, and sounds like the FDA is on board with the surrogate endpoint. Could be big validation for BridgeBio’s rare disease strategy.

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